We are scientific pioneers with unlimited potential to cure genetic disease. Our next-generation platform allows us to target any genomic sequence and develop life-changing therapies for the most challenging genetic disorders.
Our Platform
We are scientists and leaders on a shared mission to make innovative, curative therapies available to patients with devastating genetic diseases.
We are guided by curiosity, rigor, and integrity. We believe in discovery and unlimited potential. We care about science and the lives of patients.
To pave the way to faster, safer, gene editing therapeutics that cure disease and improve patient lives.
To rewrite the future by curing disease, making any edit, anywhere.
